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Results 1 - 6 of 7 for Nusinersen
  1. Nusinersen Injection 
    Nusinersen injection is used for the treatment of spinal muscular atrophy (an inherited condition that reduces muscle strength and movement) in infants, children, and adults. Nusinersen injection is in a class of medications called ...
    https://medlineplus.gov/druginfo/meds/a617010.html - Drugs and Supplements
  2. Gene Therapies are a Promising Path to Treating Rare Diseases From the National Institutes of Health 
    Rare Diseases/NIH MedlinePlus Magazine ... Rare Diseases ... Genes and Gene Therapy/NIH MedlinePlus Magazine ... Genes and Gene Therapy ... Most rare diseases are caused ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - External Health Links
  3. Spinal muscular atrophy 
    ... weakness progresses: Onasemnogene abeparvovec-xioi (Zolgensma) Risdiplam (Evrysdi) Nusinersen (Spinraza) These drugs work by increasing the amount ...
    https://medlineplus.gov/ency/article/000996.htm - Medical Encyclopedia
  4. Spinal Muscular Atrophy (SMA) (Muscular Dystrophy Association) - PDF  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Muscular Dystrophy Association ... PDF
    https://www.mda.org/.../2020/11/MDA_SMA_Fact_Sheet_Nov_2020.pdf - External Health Links
  5. Spinal Muscular Atrophy From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... National Institute of Neurological Disorders and Stroke ... Spinal muscular atrophy (SMA) refers to ...
    https://www.ninds.nih.gov/.../disorders/spinal-muscular-atrophy - External Health Links
  6. Spinal Muscular Atrophy (SMA) (Nemours Foundation)  
    Spinal Muscular Atrophy/Children ... Spinal Muscular Atrophy ... Nemours Foundation ... Spinal Muscular Atrophy (SMA), SMA, scoliosis, curved spine, strophy, wasting, ...
    https://kidshealth.org/en/parents/sma.html - External Health Links