Results 1 - 7 of 8 for Nusinersen
  1. Nusinersen Injection 
    Nusinersen injection is used for the treatment of spinal muscular atrophy (an inherited condition that reduces muscle strength and movement) in infants, children, and adults. Nusinersen injection is in a class of medications called ...
    https://medlineplus.gov/druginfo/meds/a617010.html - Drugs and Supplements
  2. Gene Therapies are a Promising Path to Treating Rare Diseases From the National Institutes of Health 
    Most rare diseases are caused by a defect in a single gene. Gene therapies treat diseases by replacing or changing a gene that doesn’t work with one that ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - External Health Links
  3. Spinal Muscular Atrophy From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Spinal muscular atrophy (SMA) refers to a group of hereditary diseases that can damage and kill ...
    https://www.ninds.nih.gov/.../disorders/spinal-muscular-atrophy - External Health Links
  4. Spinal muscular atrophy 
    ... weakness progresses: Onasemnogene abeparvovec-xioi (Zolgensma) Risdiplam (Evrysdi) Nusinersen (Spinraza) These drugs work by increasing the amount ...
    https://medlineplus.gov/ency/article/000996.htm - Medical Encyclopedia
  5. Spinal Muscular Atrophy (SMA) (Muscular Dystrophy Association) - PDF  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Muscular Dystrophy Association ... PDF
    https://www.mda.org/.../2020/11/MDA_SMA_Fact_Sheet_Nov_2020.pdf - External Health Links
  6. Motor Neuron Diseases From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Neuromuscular Disorders/Specifics ... Neuromuscular Disorders ... Degenerative Nerve Diseases/Start Here ... Degenerative Nerve Diseases ... National Institute of Neurological ...
    https://www.ninds.nih.gov/.../disorders/motor-neuron-diseases - External Health Links
  7. Spinal Muscular Atrophy (SMA) (Nemours Foundation)  
    Spinal Muscular Atrophy/Children ... Spinal Muscular Atrophy ... Nemours Foundation ... Spinal Muscular Atrophy (SMA), SMA, scoliosis, curved spine, strophy, wasting, ...
    https://kidshealth.org/en/parents/sma.html - External Health Links