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RISDIPLAM
- ... the muscle weakness progresses: Onasemnogene abeparvovec-xioi (Zolgensma) Risdiplam (Evrysdi) Nusinersen (Spinraza) These drugs work by increasing ...
- Spinal Muscular Atrophy (SMA) (Muscular Dystrophy Association) - PDFSpinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Muscular Dystrophy Association ... PDF
- Spinal Muscular Atrophy (National Institute of Neurological Disorders and Stroke)Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... National Institute of Neurological Disorders and Stroke ... Spinal muscular atrophy (SMA) refers to ...