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Infantile GM1 gangliosidoses
- Leukodystrophies/Specifics ... Leukodystrophies ... Genetic Brain Disorders/Specifics ... Genetic Brain Disorders ... Tay-Sachs Disease/Related Issues ... Tay-Sachs Disease ... Lipid ...
- ... Tifft CJ. The natural history of Type 1 infantile GM1 gangliosidosis: A literature-based ... Natural History and Progress toward Therapy. Pediatr Endocrinol ...