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  1. Resource Bibliography - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117228
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Tesmoingt C, Lidove O, Reberga A, et al. Enzyme therapy in Fabry disease: severe adverse events associated with ...
  2. Findings - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117223
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Next > Findings Guiding Question 1. What FDA-approved enzyme-replacement therapy (ERT) products are available for lysosomal storage diseases ( ...
  3. Appendix References - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117215
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Grabowski GA, Barton NW, Pastores G, et al. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of ...
  4. Methods - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117220
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Ratko TA, Marbella A, Godfrey S, et al. Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Rockville (MD): Agency ...
  5. Gaucher Disease - GeneReviews® - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK1269
    ... i.e., combined ERT and BMT or SRT). Enzyme Replacement Therapy Enzyme replacement therapy (ERT) is based on the ... al 2012 , Marshall et al 2016 ]. Chaperone-mediated enzyme enhancement therapy. Pharmacologic chaperones, competitive reversible active site inhibitors, serve ...
  6. MedlinePlus Drug Information: Miglustat 
    https://medlineplus.gov/druginfo/meds/a604015.html
    ... and who have not been improving on their enzyme therapy. Miglustat is in a class of medications called enzyme inhibitors. It works by preventing the body from ...
  7. MedlinePlus Drug Information: Cipaglucosidase alfa-atga 
    https://medlineplus.gov/druginfo/meds/a623057.html
    ... and who have not been improving on their enzyme therapy. Cipaglucosidase alfa-atga is in a class of medications called recombinant lysosomal enzymes. It works by helping break glycogen down to ...
  8. Mucopolysaccharidosis Type I - GeneReviews® - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK1162
    ... vascularity of bone tissues [ Taylor et al 2008 ]. Enzyme Replacement Therapy (ERT) Laronidase (Aldurazyme ® ) is currently licensed in the ... O, Volpi N. Effect of 6 years of enzyme replacement therapy on plasma and urine glycosaminoglycans in attenuated MPS ...
  9. Gonzalez Regimen (PDQ®) - PDQ Cancer Information Summaries - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK65848
    ... April 11, 2016. Gonzalez NJ: Pancreatic cancer, proteolytic enzyme therapy and detoxification [excerpts]. Clinical Pearls News November 1999. ... April 11, 2016. Gonzalez NJ: Pancreatic cancer, proteolytic enzyme therapy and detoxification [excerpts]. Clinical Pearls News November 1999. ...
  10. Other monitoring, assessment and management - Cystic Fibrosis - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK535679
    ... signs suggesting malabsorption occur. 102. Offer oral pancreatic enzyme replacement therapy to people with exocrine pancreatic insufficiency. Adjust the ...
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