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  1. Background - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117221
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... strong. 4 Therapeutic Measures for Lysosomal Storage Diseases Enzyme-Replacement Therapy Within the United States, the term “enzyme replacement ...
  2. Resource Bibliography - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117228
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Tesmoingt C, Lidove O, Reberga A, et al. Enzyme therapy in Fabry disease: severe adverse events associated with ...
  3. Findings - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117223
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Next > Findings Guiding Question 1. What FDA-approved enzyme-replacement therapy (ERT) products are available for lysosomal storage diseases ( ...
  4. Appendix References - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117215
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Grabowski GA, Barton NW, Pastores G, et al. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of ...
  5. Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117219
    ... of Medicine, National Institutes of Health. < Prev Next > Enzyme-Replacement Therapies for Lysosomal Storage Diseases Technical Briefs, No. 12 ... systems involved, and the degree of impairment. However, enzyme-replacement therapy (ERT) is now commercially available for six LSDs, ...
  6. Appendix Data Abstraction Tables - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117227
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... B Appendix Data Abstraction Tables Clinical Trials of Enzyme Replacement Therapy for Lysosomal Storage Diseases (MS Word, 67K) Copyright ...
  7. Summary and Implications - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117214
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Ratko TA, Marbella A, Godfrey S, et al. Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Rockville (MD): Agency ...
  8. Methods - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117220
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Ratko TA, Marbella A, Godfrey S, et al. Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Rockville (MD): Agency ...
  9. Electronic Database Search Strategies - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117225
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Ratko TA, Marbella A, Godfrey S, et al. Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Rockville (MD): Agency ...
  10. Summaries of Unpublished Studies - Enzyme-Replacement Therapies for Lysosomal Storage Diseases - NCBI Bookshelf 
    https://www.ncbi.nlm.nih.gov/books/NBK117222
    ... Quality (US); 2013 Jan. (Technical Briefs, No. 12.) Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Show details Technical ... Ratko TA, Marbella A, Godfrey S, et al. Enzyme-Replacement Therapies for Lysosomal Storage Diseases [Internet]. Rockville (MD): Agency ...
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