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Cerliponase alfa
- Cerliponase alfa is used to slow the loss of being able to crawl or walk in children with ... also known as tripeptidyl peptidase 1 (TPP1) deficiency. Cerliponase alfa is in a class of medications called enzymes. ...
- Neuronal Ceroid Lipofuscinosis (Batten Disease)
(National Institute of Neurological Disorders and Stroke)
Neuronal ceroid lipofuscinoses (NCLs), also known as Batten disease, is the name for a group of rare inherited neurodegenerative disorders that most often ...