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Results 1 - 2 of 2 for Nusinersen
  1. Gene Therapies are a Promising Path to Treating Rare Diseases From the National Institutes of Health 
    Rare Diseases/NIH MedlinePlus Magazine ... Rare Diseases ... Genes and Gene Therapy/NIH MedlinePlus Magazine ... Genes and Gene Therapy ... Most rare diseases are caused ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - External Health Links
  2. Spinal Muscular Atrophy From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Spinal muscular atrophy (SMA) refers to a group of hereditary diseases which affect motor neurons. ...
    https://www.ninds.nih.gov/.../disorders/spinal-muscular-atrophy - External Health Links