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Muscular atrophy
- Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Spinal muscular atrophy (SMA) refers to a group of hereditary diseases which affect motor neurons. ...
- Spinal Muscular Atrophy/Genetics ... Spinal Muscular Atrophy ... National Human Genome Research Institute ... From the National Institutes of Health ... Spinal muscular atrophy ...
- Spinal Muscular Atrophy/Clinical Trials ... Spinal Muscular Atrophy
- ... gene therapies to treat rare diseases like spinal muscular atrophy and Duchenne muscular dystrophy.
- Muscular Dystrophy: Other FAQs
(Eunice Kennedy Shriver National Institute of Child Health and Human Development)
Muscular Dystrophy/Living With ... Muscular Dystrophy ... Find answers to other common questions about MD, such as whether newborns can be screened for the condition. - Neuromuscular Disorders/Specifics ... Neuromuscular Disorders ... Degenerative Nerve Diseases/Start Here ... Degenerative Nerve Diseases ... National Institute of Neurological ...
- Neuromuscular Disorders/Specifics ... Neuromuscular Disorders ... Eye Diseases/Specifics ... Eye Diseases ... National Center for Advancing Translational Sciences ... From the ...
- Muscular Dystrophy/Start Here ... Muscular Dystrophy ... National Institute of Neurological Disorders and Stroke ... Muscular dystrophy (MD) refers to a group of genetic ...
- Neurofibromatosis/Start Here ... Neurofibromatosis ... National Human Genome Research Institute ... From the National Institutes of Health ... Neurofibromatosis is a genetic ...
- Leukodystrophies/Specifics ... Leukodystrophies ... Genetic Brain Disorders/Specifics ... Genetic Brain Disorders ... Tay-Sachs Disease/Related Issues ... Tay-Sachs Disease ... Lipid ...