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Results 1 - 2 of 2 for "Gm2-gangliosidosis," adult
  1. ... D, Caillaud C, Nadjar Y. Natural History of Adult Patients with GM2 Gangliosidosis. Ann Neurol. 2020 Apr;87(4):609-617. ...
  2. ... to as a lysosomal storage disorder or a GM2-gangliosidosis. Sandhoff disease is one of three conditions caused ... two conditions are called Tay-Sachs disease and GM2-gangliosidosis, AB variant, which are caused by variants in ...