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Results 1 - 1 of 1 for Atrophic muscular disease
  1. What is gene therapy?: MedlinePlus Genetics 
    ... being used to treat a small number of diseases, including an eye disorder called Leber congenital amaurosis and a muscle disorder called spinal muscular atrophy . Many more gene therapies are undergoing research to ...
    https://medlineplus.gov/genetics/understanding/therapy/genetherapy - Genetics