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Sanfilippo syndrome
- Sanfilippo Syndrome (For Parents) (Nemours Foundation)Carbohydrate Metabolism Disorders/Children ... Carbohydrate Metabolism Disorders ... Nemours Foundation
- Disease Treatments (American Society of Gene & Cell Therapy)Genes and Gene Therapy/Specifics ... Genes and Gene Therapy ... American Society of Gene & Cell Therapy
- MPS Diseases (National MPS Society)... is MPS? Learn more about rare diseases including Sanfilippo syndrome, Hunter syndrome, and Hurler syndrome
- Mucopolysaccharidoses (National Institute of Neurological Disorders and Stroke)Carbohydrate Metabolism Disorders/Specifics ... Carbohydrate Metabolism Disorders ... National Institute of Neurological Disorders and Stroke ... Mucopolysaccharidoses ...
- Neuronal Ceroid Lipofuscinosis (Batten Disease) (National Institute of Neurological Disorders and Stroke)Degenerative Nerve Diseases/Specifics ... Degenerative Nerve Diseases ... Genetic Brain Disorders/Specifics ... Genetic Brain Disorders ... National Institute of Neurological ...