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Results 1 - 4 of 4 for Nusinersen
  1. Gene Therapies are a Promising Path to Treating Rare Diseases From the National Institutes of Health 
    Rare Diseases/NIH MedlinePlus Magazine ... Rare Diseases ... Genes and Gene Therapy/NIH MedlinePlus Magazine ... Genes and Gene Therapy ... Most rare diseases are caused ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - External Health Links
  2. Spinal Muscular Atrophy (SMA) (Muscular Dystrophy Association) - PDF  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Muscular Dystrophy Association ... PDF
    https://www.mda.org/.../2020/11/MDA_SMA_Fact_Sheet_Nov_2020.pdf - External Health Links
  3. Spinal Muscular Atrophy From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Spinal muscular atrophy (SMA) refers to a group of hereditary diseases which affect motor neurons. ...
    https://www.ninds.nih.gov/.../disorders/spinal-muscular-atrophy - External Health Links
  4. Spinal Muscular Atrophy (SMA) (Nemours Foundation)  
    Spinal Muscular Atrophy/Children ... Spinal Muscular Atrophy ... Nemours Foundation ... Spinal Muscular Atrophy (SMA), SMA, scoliosis, curved spine, strophy, wasting, ...
    https://kidshealth.org/en/parents/sma.html - External Health Links