- ... AND T. R. CECH - Expression of the Murine Duchenne Muscular Dystrophy Gene in Muscle and Brain: J. S. CHAMBERIAIN, J. ... E. RANIER, A. A. REEVES, C. T. CASKEY | Duchenne Muscular Dystrophy Gene Expression in Normal and Diseased Human Muscle: ...
- NLM Digital Collections - Rare diseases. Although limited, available evidence suggests medical and other costs can be ...Publication: Washington, DC : United States Government Accountability Office, October 2021... is generally a chronic, progressive, and potentially life- Duchenne muscular dystrophy. Duchenne threatening disease. The age of symptom onset ... affect people of any childhood. Most children with Duchenne muscular dystrophy use a wheelchair by their age. They can ...
- NLM Digital Collections - Strengthening the accelerated approval pathway : an analysis of potential policy reforms and ....Publication: [Boston, Massachusetts] : Institute for Clinical and Economic Review, April 26, 2021... to market this treatment as the first for Duchenne Muscular Dystrophy (DMD). The excitement in the patient community was ... to market this treatment as the first for Duchenne Muscular Dystrophy (DMD). The excitement in the patient community was ...
- ... 3): 175-8 PSYCHOLOGY Screening the newborn for Duchenne muscular dystrophy: parents’ views. Firth MA, et al. Br Med ... 285(6345):863—5 Screening the newborn for Duchenne muscular dystrophy: parents’ views. Firth MA, et al. Br Med ...
- ... knee-ankle-foot orthoses in the treatment of Duchenne muscular dystrophy. I.M.Siegel. Arch Phys Med Rehabil 56: ... system for a family coping with chronic illness: Duchenne muscular dystrophy. D. Kaplan and J.S.Mearig. Rehabil Lit 38: ...
- ... Oct 78 Lifelong care of the child with Duchenne muscular dystrophy. Brady MH. MCN 4(4):227-30, Jul- ... Spring 79 Lifelong care of the child with Duchenne muscular dystrophy. Brady MH. MCN 4(4):227-30, Jul- ...
- ... 3 Psychosocial aspects of death and dying in Duchenne muscular dystrophy. Madorsky JG, et al. Arch Phys Med Rehabil ... 3 Psychosocial aspects of death and dying in Duchenne muscular dystrophy. Madorsky JG, et al. Arch Phys Med Rehabil ...
- ... from the French experience in the case of Duchenne muscular dystrophy. Hirtzlin I. Health Policy 1996 Jan;35(l): ... from the French experience in the case of Duchenne muscular dystrophy. Hirtzlin I. Health Policy 1996 Jan;35(l): ...
- NLM Digital Collections - Annual report - National Eye Institute (1993)Publication: [Bethesda, Md.] : National Eye Institute... characterization of mutations include Usher syndrome, myotonic dystrophy, Duchenne muscular dystrophy. Long QT syndrome, cataracts, and a variety of ... of the male and female mutation rates in Duchenne muscular dystrophy (DMD). Hum Genet 89:204- 206, 1992. Nickerson ...
- NLM Digital Collections - FDA oversightPublication: [Toronto, Ontario] : Thomson Reuters, 20-December-2021... and Co. FDA Approves Targeted Treatment for Rare Duchenne Muscular Dystrophy Mutation On February 25, 2021, the FDA granted ... Amondys 45 (casimersen) injection for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation ...
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