- NLM Digital Collections - Duchenne muscular dystrophy and related dystrophinopathies : developing drugs for treatmentPublication: Silver Spring, MD : Center for Drug Evaluation and Research, February 2018Duchenne muscular dystrophy and related dystrophinopathies : developing drugs for treatment ... Duchenne muscular dystrophy and related dystrophinopathies : developing drugs for treatment Guidance for industry United States. Department of Health and ...
- NLM Digital Collections - Rare diseases. Although limited, available evidence suggests medical and other costs can be ...Publication: Washington, DC : United States Government Accountability Office, October 2021... is generally a chronic, progressive, and potentially life- Duchenne muscular dystrophy. Duchenne threatening disease. The age of symptom onset ... affect people of any childhood. Most children with Duchenne muscular dystrophy use a wheelchair by their age. They can ...
- NLM Digital Collections - Genetic counseling on the hereditary neuromuscular diseasesPublication: [Bethesda, Md.] : The Institute ; [Atlanta : for loan by National Medical Audiovisual Center ; Washington : for sale by National Audiovisual Center], 1976... lists neuromuscular diseases with excellent inheritance. They are Duchenne, muscular dystrophy, both of the severe type and of the ... of carrier state and relatives of patients with Duchenne muscular dystrophy. The next slide shows a family shows criteria ...
- ... AND T. R. CECH - Expression of the Murine Duchenne Muscular Dystrophy Gene in Muscle and Brain: J. S. CHAMBERIAIN, J. ... E. RANIER, A. A. REEVES, C. T. CASKEY | Duchenne Muscular Dystrophy Gene Expression in Normal and Diseased Human Muscle: ...
- NLM Digital Collections - Approaches to floppy babies and weak children and genetic counselingPublication: [Bethesda, Md.] : The Institute, 1976... the most frequent of all neuromuscular diseases, namely Duchenne muscular dystrophy. Duchenne muscular dystrophy in my muscle clinic, which really presents a ...
- NLM Digital Collections - Strengthening the accelerated approval pathway : an analysis of potential policy reforms and ....Publication: [Boston, Massachusetts] : Institute for Clinical and Economic Review, April 26, 2021... to market this treatment as the first for Duchenne Muscular Dystrophy (DMD). The excitement in the patient community was ... to market this treatment as the first for Duchenne Muscular Dystrophy (DMD). The excitement in the patient community was ...
- ... 3): 175-8 PSYCHOLOGY Screening the newborn for Duchenne muscular dystrophy: parents’ views. Firth MA, et al. Br Med ... 285(6345):863—5 Screening the newborn for Duchenne muscular dystrophy: parents’ views. Firth MA, et al. Br Med ...
- ... knee-ankle-foot orthoses in the treatment of Duchenne muscular dystrophy. I.M.Siegel. Arch Phys Med Rehabil 56: ... system for a family coping with chronic illness: Duchenne muscular dystrophy. D. Kaplan and J.S.Mearig. Rehabil Lit 38: ...
- ... Oct 78 Lifelong care of the child with Duchenne muscular dystrophy. Brady MH. MCN 4(4):227-30, Jul- ... Spring 79 Lifelong care of the child with Duchenne muscular dystrophy. Brady MH. MCN 4(4):227-30, Jul- ...
- ... 3 Psychosocial aspects of death and dying in Duchenne muscular dystrophy. Madorsky JG, et al. Arch Phys Med Rehabil ... 3 Psychosocial aspects of death and dying in Duchenne muscular dystrophy. Madorsky JG, et al. Arch Phys Med Rehabil ...
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