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7 results
  1. NLM Digital Collections - Betibeglogene autotemcel for beta thalassemia : effectiveness and value : final evidence ... 
    Publication: [Boston, Massachusetts] : Institute for Clinical and Economic Review, July 19, 2022
    ... have also been reported in patients with cerebral adrenoleukodystrophy treated with elivaldogene autotemcel; at least one case ... Application for eli-cel Gene Therapy for Cerebral Adrenoleukodystrophy (CALD) in Patients Without a Matched Sibling Donor. ...
  2. NLM Digital Collections - National Library of Medicine classification : a scheme for the shelf arrangement of library ... 
    Publication: Bethesda, Md. : U.S. Dept. of Health and Human Services, Public Health Service, National Institutes of Health, National Library of Medicine ; Washington, DC : For sale by the Supt. of Docs., U.S. G.P.O., 1999
    ... see Corticotropin Adrenogenital Syndrome see Adrenal Hyperplasia, Congenital Adrenoleukodystrophy WD 205.5.L5 Adrenoleukodystrophy, Neonatal see Peroxisomal ...
  3. ... see Corticotropin Adrenogenital Syndrome see Adrenal Hyperplasia, Congenital Adrenoleukodystrophy WD 205.5.L5 Adrenolytics see Adrenergic Agents Adrenomimetics see Adrenergic Agents Adrenomyeloneuropathy see ... see Doxorubicin Adsorbents see Dermatologic Agents; Gastrointestinal ...
  4. ... a form of “‘elephant man's dis- ease'’) . B Adrenoleukodystrophy sis (Lou Gehrig's disease) . ease-fighting antibodies) . (another ... the case; and expanding and enhancing the traditional reference, research assistance, coding, and retrieval activities of the ...
  5. NLM Digital Collections - Analysis of supply, distribution, demand, and access issues associated with immune globulin ... 
    Publication: Washington, D.C. : U.S. Department of Health and Human Services, Office of the Assistant Secretary for Planning and Evaluation, 2007
    ... with monoclonal IgM A – at least one randomized Adrenoleukodystrophy controlled study Amyotrophic lateral sclerosis Unlikely to be ... from IGIV Count (Percent) Patient Type # of Infusions References Mild Moderate Severe Aghamohammadi et Children with PI ...
  6. NLM Digital Collections - Quality of healthcare 
    Publication: [Toronto, Ontario] : Thomson Reuters, 20-December-2021
    ... Disease), Mucopolysaccharidosis Type 1 (MPS1), and X-linked Adrenoleukodystrophy (XALD) to the Colorado newborn screening panel. * 2021 ... other documents, provider manuals or policies incorporated by reference in such contract, and (B) a right to ...