Skip navigation

Official websites use .gov
A .gov website belongs to an official government organization in the United States.

Secure .gov websites use HTTPS
A lock ( ) or https:// means you’ve safely connected to the .gov website. Share sensitive information only on official, secure websites.

Results 1 - 3 of 3 for spinal muscular atrophy
  1. What is gene therapy?: MedlinePlus Genetics 
    ... Leber congenital amaurosis and a muscle disorder called spinal muscular atrophy . Many more gene therapies are undergoing research to ...
    https://medlineplus.gov/genetics/understanding/therapy/genetherapy - Genetics
  2. Is gene therapy safe?: MedlinePlus Genetics 
    ... therapies, including therapies to treat inherited disorders like spinal muscular atrophy and Leber congenital amaurosis . Learn how to cite ...
    https://medlineplus.gov/genetics/understanding/therapy/safety - Genetics
  3. Is gene therapy available to treat my disorder?: MedlinePlus Genetics 
    ... as melanoma , and a genetic muscle condition called spinal muscular atrophy . Other genetic therapies have been approved for blood ...
    https://medlineplus.gov/genetics/understanding/therapy/availability - Genetics