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Results 1 - 10 of 17 for Trials
  1. Is gene therapy available to treat my disorder?: MedlinePlus Genetics 
    ... in other countries. Hundreds of research studies (clinical trials) are under way to test gene therapy as ... you are interested in participating in a clinical trial, talk with your doctor or a genetics professional ...
    https://medlineplus.gov/genetics/understanding/therapy/availability - Genetics
  2. Is gene therapy safe?: MedlinePlus Genetics 
    The first gene therapy trial was run more than thirty years ago. The earliest studies showed that gene therapy could have very serious health risks, ... working to ensure that gene therapy research, clinical trials, and approved treatments are as safe as possible. ...
    https://medlineplus.gov/genetics/understanding/therapy/safety - Genetics
  3. Leber congenital amaurosis 
    ... congenital amaurosis: clinical correlations with genotypes, gene therapy trials update, and future directions. J AAPOS. 2009 Dec; ... s congenital amaurosis: a phase 1 dose-escalation trial. Lancet. 2009 Nov 7;374(9701):1597-605. ...
    https://medlineplus.gov/.../condition/leber-congenital-amaurosis - Genetics
  4. Nearsightedness 
    ... Hosseini SM, Paterson AD; Diabetes Control and Complications Trial/Epidemiology of Diabetes Interventions, and Complications Research Group; ... Ong RT, Doring A; Diabetes Control and Complications Trial/Epidemiology of Diabetes Interventions and Complications (DCCT/EDIC) ...
    https://medlineplus.gov/genetics/condition/nearsightedness - Genetics
  5. How are genetic conditions treated or managed?: MedlinePlus Genetics 
    ... for genetic conditions, are under study in clinical trials. Learn how to cite this page
    https://medlineplus.gov/genetics/understanding/consult/treatment - Genetics
  6. Lennox-Gastaut syndrome 
    ... a consensus approach on diagnosis, assessment, management, and trial methodology. Lancet Neurol. 2009 Jan;8(1):82- ...
    https://medlineplus.gov/genetics/condition/lennox-gastaut-syndrome - Genetics
  7. What are genome editing and CRISPR-Cas9?: MedlinePlus Genetics 
    ... It is being explored in research and clinical trials for a wide variety of diseases, including single- ...
    https://medlineplus.gov/.../genomicresearch/genomeediting - Genetics
  8. GRN-related frontotemporal lobar degeneration 
    ... frontotemporal dementia: NIH-EXAMINER as a potential clinical trial endpoint. Alzheimers Dement. 2020 Jan;16(1):11- ...
    https://medlineplus.gov/...related-frontotemporal-lobar-degeneration - Genetics
  9. What is pharmacogenomics?: MedlinePlus Genetics 
    ... and new approaches are under study in clinical trials. In the future, pharmacogenomics will be used to ...
    https://medlineplus.gov/.../genomicresearch/pharmacogenomics - Genetics
  10. Niemann-Pick disease 
    ... A Niemann-Pick disease: possible endpoints for therapeutic trials. Neurology. 2006 Jan 24;66(2):228-32. ...
    https://medlineplus.gov/genetics/condition/niemann-pick-disease - Genetics
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