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Results 1 - 1 of 1 for SMA
  1. Gene therapies are a promising path to treating rare diseases | NIH MedlinePlus Magazine 
    ... on gene therapies to treat rare diseases like spinal muscular atrophy and Duchenne muscular dystrophy. ... and development on gene therapies to treat them. Spinal muscular atrophy: Genetic therapies to improve movement A medication called ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - MedlinePlus Magazine