Skip navigation

Official websites use .gov
A .gov website belongs to an official government organization in the United States.

Secure .gov websites use HTTPS
A lock ( ) or https:// means you’ve safely connected to the .gov website. Share sensitive information only on official, secure websites.

Results 1 - 10 of 52 for Gene therapy
  1. Gene therapies are a promising path to treating rare diseases | NIH MedlinePlus Magazine 
    ... caused by a defect in a single gene. Gene therapies treat diseases by replacing or changing a gene ... that does. NIH supports research and development on gene therapies to treat rare diseases like spinal muscular atrophy ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - MedlinePlus Magazine
  2. Tesha Samuels advocates for others after living with sickle cell disease | NIH MedlinePlus Magazine 
    ... Samuels What was your treatment like before undergoing gene therapy? My treatment plan included a lot of pain ... to 36. Can you describe your experience undergoing gene therapy? Gene therapy was a beautiful blessing, but between ...
    https://magazine.medlineplus.gov/...-living-with-sickle-cell-disease - MedlinePlus Magazine
  3. Updates from NIH’s sickle cell disease scientists | NIH MedlinePlus Magazine 
    ... and Dr. John Tisdale discuss bone marrow transplants, gene therapy Many people with sickle cell disease (SCD) are ... cure through expanded bone marrow transplant treatment and gene therapy. "The majority of patients with SCD are still ...
    https://magazine.medlineplus.gov/...s-sickle-cell-disease-scientists - MedlinePlus Magazine
  4. NIH MedlinePlus Magazine Multimedia 
    ... Source: Substance Abuse and Mental Health Services Administration Gene Therapies 7K There are about 7,000 known rare ...
    https://magazine.medlineplus.gov/multimedia/health-fast-facts - MedlinePlus Magazine
  5. The costs of living with sickle cell disease in the United States | NIH MedlinePlus Magazine 
    ... the financial burden on people living with it. Gene therapies and treatments could greatly reduce the current costs ... initiative has also announced the launch of the Gene therapy to Reduce All Sickle Pain (GRASP) Trial , which ...
    https://magazine.medlineplus.gov/...ell-disease-in-the-united-states - MedlinePlus Magazine
  6. Sickle cell disease: What you should know | NIH MedlinePlus Magazine 
    ... growing option for people with sickle cell disease. Gene Therapy and Gene Editing: The National Heart, Lung, and ... study to test the effects of an experimental gene therapy to treat sickle cell disease that involves removing ...
    https://magazine.medlineplus.gov/...ell-disease-what-you-should-know - MedlinePlus Magazine
  7. Is a widely available cure for sickle cell disease on the horizon? | NIH MedlinePlus Magazine 
    ... On May 30, 2017, Dasu underwent an experimental gene therapy procedure at the NIH Clinical Center on the ...
    https://magazine.medlineplus.gov/...ckle-cell-disease-on-the-horizon - MedlinePlus Magazine
  8. Meet the Director: Gary H. Gibbons, M.D., National Heart, Lung, and Blood Institute | NIH MedlinePlus Magazine 
    ... sickle cell disease initiative is taking advantage of gene therapy and gene editing. The technology exists to take genetic code ...
    https://magazine.medlineplus.gov/...l-heart-lung-and-blood-institute - MedlinePlus Magazine
  9. Breaking new ground: NIH research highlights | NIH MedlinePlus Magazine 
    ... scientists showed the approach holds promise as a gene therapy for three diseases in animal or cell models: ...
    https://magazine.medlineplus.gov/...w-ground-nih-research-highlights - MedlinePlus Magazine
  10. Learn about your genes with MedlinePlus | NIH MedlinePlus Magazine 
    ... you can read straightforward information about genetic testing, gene therapy, and genetic research. The handbook also covers: Clear definitions of genetic terms, such as genes and DNA An explanation of gene variants and ...
    https://magazine.medlineplus.gov/...bout-your-genes-with-medlineplus - MedlinePlus Magazine
previous · 1 · 2 · 3 · 4 · 5 · 6 · next