Skip navigation

Official websites use .gov
A .gov website belongs to an official government organization in the United States.

Secure .gov websites use HTTPS
A lock ( ) or https:// means you’ve safely connected to the .gov website. Share sensitive information only on official, secure websites.

Results 1 - 2 of 2 for Duchenne muscular dystrophy
  1. ... treat rare diseases like spinal muscular atrophy and Duchenne muscular dystrophy. ... other neurological disorders including other rare muscular disorders. Duchenne muscular dystrophy: Genetic therapies to improve muscle weakness Muscular dystrophies ...
  2. ... for three diseases in animal or cell models: Duchenne muscular dystrophy (in mice); sickle cell disease (in blood stem ...