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Results 1 - 10 of 10 for clinical trials
  1. Is gene therapy available to treat my disorder?: MedlinePlus Genetics 
    ... approved in other countries. Hundreds of research studies (clinical trials) are under way to test gene therapy as ... If you are interested in participating in a clinical trial, talk with your doctor or a genetics professional ...
    https://medlineplus.gov/genetics/understanding/therapy/availability - Genetics
  2. Is gene therapy safe?: MedlinePlus Genetics 
    ... are working to ensure that gene therapy research, clinical trials, and approved treatments are as safe as possible. ... protect people who participate in research studies (called clinical trials). The U.S. Food and Drug Administration (FDA) ...
    https://medlineplus.gov/genetics/understanding/therapy/safety - Genetics
  3. GRN-related frontotemporal lobar degeneration 
    ... familial frontotemporal dementia: NIH-EXAMINER as a potential clinical trial endpoint. Alzheimers Dement. 2020 Jan;16(1):11-21. doi: 10.1016/j.jalz.2019.01.012. Citation on PubMed or Free article on PubMed ... genetic, and pathologic characteristics of patients with frontotemporal ...
    https://medlineplus.gov/...related-frontotemporal-lobar-degeneration - Genetics
  4. How are genetic conditions treated or managed?: MedlinePlus Genetics 
    ... approaches for genetic conditions, are under study in clinical trials. Learn how to cite this page
    https://medlineplus.gov/genetics/understanding/consult/treatment - Genetics
  5. What are genome editing and CRISPR-Cas9?: MedlinePlus Genetics 
    ... people . It is being explored in research and clinical trials for a wide variety of diseases, including single- ...
    https://medlineplus.gov/.../genomicresearch/genomeediting - Genetics
  6. What is pharmacogenomics?: MedlinePlus Genetics 
    ... growing, and new approaches are under study in clinical trials. In the future, pharmacogenomics will be used to ...
    https://medlineplus.gov/.../genomicresearch/pharmacogenomics - Genetics
  7. Leber congenital amaurosis 
    ... PubMed Chung DC, Traboulsi EI. Leber congenital amaurosis: clinical correlations with genotypes, gene therapy trials update, and future directions. J AAPOS. 2009 Dec; ...
    https://medlineplus.gov/.../condition/leber-congenital-amaurosis - Genetics
  8. Dentatorubral-pallidoluysian atrophy 
    ... natural history and developing biomarkers to accelerate therapeutic trials in ... Molecular basis for wide clinical features of DRPLA. Clin Neurosci. 1995;3(1): ...
    https://medlineplus.gov/.../dentatorubral-pallidoluysian-atrophy - Genetics
  9. Niemann-Pick disease 
    ... A Niemann-Pick disease: possible endpoints for therapeutic trials. Neurology. 2006 Jan 24;66(2):228-32. ... Pick disease type C symptomatology: an expert-based clinical description. Orphanet J Rare Dis. 2013 Oct 17; ...
    https://medlineplus.gov/genetics/condition/niemann-pick-disease - Genetics
  10. Age-related macular degeneration 
    ... WL; Complications of Age-Related Macular Degeneration Prevention Trial Research Group; Brucker AJ, Orlin A, Brown G, ... Ratnapriya R, Chew EY. Age-related macular degeneration-clinical review and genetics update. Clin Genet. 2013 Aug; ...
    https://medlineplus.gov/.../age-related-macular-degeneration - Genetics