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- Genes and Gene Therapy/NIH MedlinePlus Magazine ... Genes and Gene Therapy ... Rare Diseases/NIH MedlinePlus Magazine ... Rare Diseases ... Most rare diseases are caused ...
- Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... National Institute of Neurological Disorders and Stroke ... Spinal muscular atrophy (SMA) refers to ...