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Results 1 - 3 of 3 for Leber optic atrophy
  1. Leber hereditary optic neuropathy 
    ... children. Hereditary optic neuroretinopathy Leber hereditary optic atrophy Leber optic atrophy Leber's hereditary optic neuropathy Leber's optic ... Leber's optic neuropathy LHON Genetic Testing Registry: Leber optic atrophy Leber hereditary optic neuropathy National Organization for Rare ...
    https://medlineplus.gov/.../leber-hereditary-optic-neuropathy - Genetics
  2. What is gene therapy?: MedlinePlus Genetics 
    ... treat a small number of diseases, including an eye disorder called Leber congenital amaurosis and a muscle disorder called spinal muscular atrophy . Many more gene therapies are undergoing research to ...
    https://medlineplus.gov/genetics/understanding/therapy/genetherapy - Genetics
  3. Is gene therapy available to treat my disorder?: MedlinePlus Genetics 
    ... are available for conditions that include a rare eye disorder called Leber congenital amaurosis , a form of skin cancer known as melanoma , and a genetic muscle condition called spinal muscular atrophy . Other genetic therapies have been approved for blood ...
    https://medlineplus.gov/genetics/understanding/therapy/availability - Genetics