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Results 1 - 3 of 3 for Leber congenital amaurosis
  1. What is gene therapy?: MedlinePlus Genetics 
    ... number of diseases, including an eye disorder called Leber congenital amaurosis and a muscle disorder called spinal muscular atrophy . ...
    https://medlineplus.gov/genetics/understanding/therapy/genetherapy - Genetics
  2. Is gene therapy safe?: MedlinePlus Genetics 
    ... treat inherited disorders like spinal muscular atrophy and Leber congenital amaurosis . Learn how to cite this page
    https://medlineplus.gov/genetics/understanding/therapy/safety - Genetics
  3. Is gene therapy available to treat my disorder?: MedlinePlus Genetics 
    ... conditions that include a rare eye disorder called Leber congenital amaurosis , a form of skin cancer known as melanoma , ...
    https://medlineplus.gov/genetics/understanding/therapy/availability - Genetics