Skip navigation

Official websites use .gov
A .gov website belongs to an official government organization in the United States.

Secure .gov websites use HTTPS
A lock ( ) or https:// means you’ve safely connected to the .gov website. Share sensitive information only on official, secure websites.

Results 1 - 5 of 6 for Nusinersen
  1. Nusinersen Injection 
    Nusinersen injection is used for the treatment of spinal muscular atrophy (an inherited condition that reduces muscle strength and movement) in infants, children, and adults. Nusinersen injection is in a class of medications called ...
    https://medlineplus.gov/druginfo/meds/a617010.html - Drugs and Supplements
  2. Spinal Muscular Atrophy From the National Institutes of Health (National Institute of Neurological Disorders and Stroke)  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... National Institute of Neurological Disorders and Stroke ... Spinal muscular atrophy (SMA) refers to ...
    https://www.ninds.nih.gov/.../disorders/spinal-muscular-atrophy - External Health Links
  3. Spinal muscular atrophy 
    ... weakness progresses: Onasemnogene abeparvovec-xioi (Zolgensma) Risdiplam (Evrysdi) Nusinersen (Spinraza) These drugs work by increasing the amount ...
    https://medlineplus.gov/ency/article/000996.htm - Medical Encyclopedia
  4. Spinal Muscular Atrophy (SMA) (Muscular Dystrophy Association) - PDF  
    Spinal Muscular Atrophy/Start Here ... Spinal Muscular Atrophy ... Muscular Dystrophy Association ... PDF
    https://www.mda.org/.../2020/11/MDA_SMA_Fact_Sheet_Nov_2020.pdf - External Health Links
  5. Gene therapies are a promising path to treating rare diseases | NIH MedlinePlus Magazine 
    ... Genetic therapies to improve movement A medication called nusinersen was one of the first genetic therapies approved ... those problems in children and adults with SMA. Nusinersen targets another gene called SMN2 that also makes ...
    https://magazine.medlineplus.gov/...g-path-to-treating-rare-diseases - MedlinePlus Magazine