... people have mutations in the gene associated with Niemann-PickdiseasetypeC1. What genes are related to Niemann-Pickdisease? ... lipids within cells as seen in people with Niemann-PickdiseasetypeC1. The NPC2 gene provides instructions to produce a ...
ghr.nlm.nih.gov/condition/niemann-pick-disease - External Health Links
... Clinical Trials: News & Updates NIH Cyclodextrin Trial
For Niemann-PickDiseaseType C ~ Pediatrics
~ UPDATE ~
Dateline: 6/ 27/2014
We received ... Orphazyme ApS of an upcoming clinical trial for Niemann-PickDiseaseType C. Orphazyme ApS (Copenhagen, Denmark) develops new therapies for ...