... survive into adulthood. The signs and symptoms of Niemann-PickdiseasetypesC1 and C2 are very similar; these types differ only in their genetic cause. Niemann-PickdiseasetypesC1 and C2 usually become apparent in childhood, although ...
ghr.nlm.nih.gov/condition/niemann-pick-disease - External Health Links
... News & Updates BREAKING NEWS NIH Cyclodextrin Trial
For Niemann-PickDiseaseType C ~ Pediatrics
~ UPDATE ~
We received ... Orphazyme ApS of an upcoming clinical trial for Niemann-PickDiseaseType C. Orphazyme ApS (Copenhagen, Denmark) develops new therapies for ...